{"id":6383,"date":"2023-10-02T15:18:40","date_gmt":"2023-10-02T18:18:40","guid":{"rendered":"https:\/\/allumiqs.com\/science\/the-analytical-scientist-defier-lincertitude-dans-la-therapie-genique\/"},"modified":"2023-11-30T15:20:48","modified_gmt":"2023-11-30T19:20:48","slug":"the-analytical-scientist-defier-lincertitude-dans-la-therapie-genique","status":"publish","type":"science","link":"https:\/\/allumiqs.com\/fr\/science\/the-analytical-scientist-defier-lincertitude-dans-la-therapie-genique\/","title":{"rendered":"The Analytical Scientist – D\u00e9fier l’incertitude dans la th\u00e9rapie g\u00e9nique"},"content":{"rendered":"\n

D\u00e9fier l’incertitude dans la th\u00e9rapie g\u00e9nique<\/h2>\n\n

Comment une nouvelle technologie bas\u00e9e sur la spectrom\u00e9trie de masse permet aux chercheurs de caract\u00e9riser les prot\u00e9ines et les effets hors cible de l’\u00e9dition de g\u00e8nes avec une sensibilit\u00e9 et une fiabilit\u00e9 accrues.<\/h4>\n\n

par Hugo Gagnon, CSO, Allumiqs<\/p>\n\n

Les progr\u00e8s r\u00e9cents en mati\u00e8re de th\u00e9rapie g\u00e9nique – tels que les outils bas\u00e9s sur CRISPR\/Cas9 – permettent aux chercheurs d’introduire ou de modifier des g\u00e8nes avec une faisabilit\u00e9 sans pr\u00e9c\u00e9dent. Ces technologies sont extr\u00eamement int\u00e9ressantes d’un point de vue th\u00e9rapeutique, en particulier pour le traitement des maladies rares et chroniques. La possibilit\u00e9 de gu\u00e9rir des maladies mortelles bas\u00e9es sur des variantes g\u00e9n\u00e9tiques, telles que la dystrophie musculaire, la mucoviscidose et la maladie de Huntington, explique le battage m\u00e9diatique autour de ces technologies. En outre, la polyvalence des approches de th\u00e9rapie g\u00e9nique semble infinie.<\/p>\n\n

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Aller \u00e0 l’article<\/a><\/div>\n<\/div>\n\n

<\/p>\n","protected":false},"excerpt":{"rendered":"

D\u00e9fier l’incertitude dans la th\u00e9rapie g\u00e9nique Comment une nouvelle technologie bas\u00e9e sur la spectrom\u00e9trie de masse permet aux chercheurs de caract\u00e9riser les prot\u00e9ines et les effets hors cible de l’\u00e9dition […]<\/p>\n","protected":false},"author":34,"featured_media":4611,"template":"","meta":{"inline_featured_image":false,"_EventAllDay":false,"_EventTimezone":"","_EventStartDate":"","_EventEndDate":"","_EventStartDateUTC":"","_EventEndDateUTC":"","_EventShowMap":false,"_EventShowMapLink":false,"_EventURL":"","_EventCost":"","_EventCostDescription":"","_EventCurrencySymbol":"","_EventCurrencyCode":"","_EventCurrencyPosition":"","_EventDateTimeSeparator":"","_EventTimeRangeSeparator":"","_EventOrganizerID":[],"_EventVenueID":[],"_OrganizerEmail":"","_OrganizerPhone":"","_OrganizerWebsite":"","_VenueAddress":"","_VenueCity":"","_VenueCountry":"","_VenueProvince":"","_VenueState":"","_VenueZip":"","_VenuePhone":"","_VenueURL":"","_VenueStateProvince":"","_VenueLat":"","_VenueLng":"","_VenueShowMap":false,"_VenueShowMapLink":false,"download_url":"","footnotes":""},"tags":[],"sciencecat":[118],"aioseo_notices":[],"_links":{"self":[{"href":"https:\/\/allumiqs.com\/fr\/wp-json\/wp\/v2\/science\/6383"}],"collection":[{"href":"https:\/\/allumiqs.com\/fr\/wp-json\/wp\/v2\/science"}],"about":[{"href":"https:\/\/allumiqs.com\/fr\/wp-json\/wp\/v2\/types\/science"}],"author":[{"embeddable":true,"href":"https:\/\/allumiqs.com\/fr\/wp-json\/wp\/v2\/users\/34"}],"version-history":[{"count":1,"href":"https:\/\/allumiqs.com\/fr\/wp-json\/wp\/v2\/science\/6383\/revisions"}],"predecessor-version":[{"id":6384,"href":"https:\/\/allumiqs.com\/fr\/wp-json\/wp\/v2\/science\/6383\/revisions\/6384"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/allumiqs.com\/fr\/wp-json\/wp\/v2\/media\/4611"}],"wp:attachment":[{"href":"https:\/\/allumiqs.com\/fr\/wp-json\/wp\/v2\/media?parent=6383"}],"wp:term":[{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/allumiqs.com\/fr\/wp-json\/wp\/v2\/tags?post=6383"},{"taxonomy":"sciencecat","embeddable":true,"href":"https:\/\/allumiqs.com\/fr\/wp-json\/wp\/v2\/sciencecat?post=6383"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}